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Phase I/II KOMET-001: First-in-Human Study of Ziftomenib, a Novel KMT2A-Menin Inhibitor, in Relapsed/Refractory AML

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Current phase Ia/Ib analysis reports manageable safety and preliminary efficacy with ziftomenib in patients with relapsed/refractory AML, with a CR rate of 30% in 20 patients with NPM1-mutated disease.

Released: December 12, 2022

Expiration: December 11, 2023

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